Unfortunately, because of how rare this is, there isn't much info or data available ... she was told told there was 'no ...

Thanks to the consistent and focused efforts of researchers and conservationists, mountain yellow-legged frogs are thriving ...

The Health Secretary also pointed to inequalities in prostate cancer diagnoses, with black men two and a half times more ...

Jumping right into the concerning situation, Austin agreed to donate his bone marrow. Luckily, the bone marrow samples ...

As of last year, Clementine was just one of 10 people who have been diagnosed with a mutation to the TLR8 gene. She received ...

In a new study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs ...

The FDA issued its first stamp of approval for a cell or gene therapy back in 2017 to Novartis' Kymriah. | The gene therapy ...

The company has decided to advance two new wholly-owned pipeline drugs, AOC 1086 and AOC 1072, targeting two rare genetic ...

As the rollout of its recently launched pulmonary arterial hypertension (PAH) drug Winrevair ramps up, Merck is continuing ...

On Wednesday, The Dallas Morning News reported that Dallas restauranteur Al Biernat died at 69 after a battle with ...

In a groundbreaking study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs diseases—two rare, often fatal lysosomal storage disorders that cause ...

Healx will use its AI-based drug discovery tech to analyze proprietary Sanofi compound data and identify potential rare disease targets.